Panel: Patient-centric by design: Creating therapies with the patient in mind

Advanced therapies hold great potential, but their real-world impact depends on how well they address the needs of human subjects across the treatment journey. Patient-focused development requires attention to safety, accessibility, and quality of life, alongside scientific and regulatory considerations. This panel discusses strategies for embedding the patient perspective into therapy design and delivery. 

Key takeaways: 

• Explore how patient input informs clinical trial design and endpoint selection. 

• Assess strategies to balance efficacy, safety margins, and quality of life. 

• Examine approaches to improve accessibility and affordability of advanced therapies. 

• Discuss methods for integrating patient-reported outcomes into R&D decisions. 

• Consider long-term monitoring frameworks that support patient well-being post-treatment.