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Clinical Trials

Texas Children’s Hospital First to Deliver a Novel Gene Therapy for Rett Syndrome
5 December 2023
Texas Children’s Hospital First to Deliver a Novel Gene Therapy for Rett Syndrome
Two female pediatric patients with
FDA Investigating ‘Serious Risk’ of Secondary Malignancy Linked to BCMA- or CD19-Directed CAR-T Immunotherapies
29 November 2023
FDA Investigating ‘Serious Risk’ of Secondary Malignancy Linked to BCMA- or CD19-Directed CAR-T Immunotherapies
FDA investigates T cell malignancy
Sernova’s Hemophilia A Program Receives Orphan Drug and Rare Pediatric Disease Designations from FDA
28 November 2023
Sernova’s Hemophilia A Program Receives Orphan Drug and Rare Pediatric Disease Designations from FDA
Sernova has announced that the
Positive Clinical Results in Myotubular Myopathy Demonstrate Impact on Respiratory and Motor Functions Amidst Severe Challenges
23 November 2023
Positive Clinical Results in Myotubular Myopathy Demonstrate Impact on Respiratory and Motor Functions Amidst Severe Challenges
Clinical results of a gene
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4 December 2023

20 Years of Advanced Therapies with David McCall: a Retrospective on Phacilitate’s Founding and Evolution of the Industry

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6 December 2023

Oxford Biomedica Acquires ABL Europe from Institut Mérieux

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5 December 2023

Texas Children’s Hospital First to Deliver a Novel Gene Therapy for Rett Syndrome

First Patient Enrolled in AskBio’s Phase I Trial for Multiple System Atrophy-Parkinsonian Type (MSA-P) Gene Therapy
22 November 2023
First Patient Enrolled in AskBio’s Phase I Trial for Multiple System Atrophy-Parkinsonian Type (MSA-P) Gene Therapy
AskBio has announced that the
Verve Therapeutics’ VERVE-101 Demonstrates Breakthrough in vivo Base Editing for Familial Hypercholesterolemia
15 November 2023
Verve Therapeutics’ VERVE-101 Demonstrates Breakthrough in vivo Base Editing for Familial Hypercholesterolemia
Verve Therapeutics shows promising reductions
AviadoBio Announces FDA Clearance of IND and Fast Track Designation for Treatment of Frontotemporal Dementia with GRN Mutations
7 November 2023
AviadoBio Announces FDA Clearance of IND and Fast Track Designation for Treatment of Frontotemporal Dementia with GRN Mutations
AviadoBio has announced that the
Sana Biotechnology Announces Shifted Focus to ex vivo Cell Therapy Platform
12 October 2023
Sana Biotechnology Announces Shifted Focus to ex vivo Cell Therapy Platform
Sana Biotechnology has announced a
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POPULAR NEWS ITEMS
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20 Years of Advanced Therapies with David McCall: a Retrospective on Phacilitate’s Founding and Evolution of the Industry

Image

Oxford Biomedica Acquires ABL Europe from Institut Mérieux

Image

Texas Children’s Hospital First to Deliver a Novel Gene Therapy for Rett Syndrome